Tim has been selected as a Genetics Medicines Co-Lead alongside Stephan Sanders to accelerate development of targeted treatements for genetic forms of profound autism.

The Center for Therapeutic Genetics: a new collaboration to develop precision medicines for those with rare diseases, using infrastructure and repeatable practices that will be shared with others.

We are excited to announce our lab, along with a consortium of collaborators lead by the Broad Institute, has been selected to receive funding from the Advanced Research Projects Agency for Health (ARPA-H) under its THRIVE program. The award will fund the Pediatric Epilepsies and Rare CNS (PERC) Gene Editing Platform.

Our latest publication in Nature Medicine describes an ASO developed for KCNT1 epilepsy